Category:Orphan drugs
From WikiMD's Food, Medicine & Wellness Encyclopedia
Lists of all drugs that have received orphan status in the United States and Europe are available from the U.S. Food and Drug Administration and the European Commission, respectively:
Pages in category "Orphan drugs"
The following 200 pages are in this category, out of 330 total.
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- Acalabrutinib
- Acetohydroxamic acid
- Actemra
- Adagrasib
- Afamelanotide
- Alglucosidase alfa
- Alpha 1 Antitrypsin deficiency
- Alpha-1-Proteinase Inhibitor (Human)
- Altretamine
- Alvocidib
- Amifampridine
- Dalfampridine
- Amitriptyline
- Anacaulase
- Anagrelide
- Anisina
- Ansuvimab-zykl
- Anti-transforming growth factor beta (TGF-ß) trap fusion protein
- Artesunate
- Asciminib
- Asfotase alfa
- Asparaginase erwinia chrysanthemi (recombinant)-rywn
- Atoltivimab, maftivimab, and odesivimab-ebgn
- Atoltivimab/maftivimab/odesivimab
- Avacopan
- Avalglucosidase alfa
- Avalglucosidase alfa-ngpt
- Avapritinib
- Avatrombopag
- Avelumab
- Axicabtagene ciloleucel
- Vidaza
B
- Baloxavir marboxil
- Belantamab mafodotin
- Belantamab mafodotin-blmf
- Belumosudil
- Belzutifan
- Benralizumab
- Berotralstat
- Bevacizumab
- Binimetinib
- Bortezomib
- Bosentan
- Brentuximab vedotin
- Brexucabtagene autoleucel
- Brigatinib
- Briumvi
- Budesonide
- Budesonide Oral Inhalation
- Buprenorphine + Naloxone
- Buprenorphine/naloxone
- Burosumab
- Busulfan
C
- Cabometyx
- Cabozantinib
- Caffeine citrate
- Calaspargase pegol
- Xywav
- Caplacizumab
- Caplacizumab-yhdp
- Capmatinib
- Carboprost
- Carglumic acid
- Carmustine
- Carmustine implant
- Casimersen
- Cerliponase alfa
- Cholic acid
- Ciltacabtagene autoleucel
- Cipaglucosidase alfa
- Cladribine
- Cobimetinib
- Colchicine
- Cometriq
- Conestat alfa
- Copper (64Cu) oxodotreotide
- Crizanlizumab
- Crizanlizumab-tmca
- Cystaran
- Cysteamine bitartrate
D
E
F
G
I
K
L
- L-asparaginase
- Lanadelumab-flyo
- Laronidase
- Larotrectinib
- Lecanemab
- Lenacapavir
- Leniolisib
- Lenvatinib
- Letermovir
- Lisocabtagene maraleucel
- Lomitapide mesylate
- Lonafarnib
- Lonapegsomatropin
- Loncastuximab tesirine-lpyl
- Lorlatinib
- Losartan
- Lovotibeglogene autotemcel
- Lumacaftor and ivacaftor
- Lumasiran
- Lurbinectedin
- Luspatercept–aamt
- Lusutrombopag
- Lutetium Lu 177 dotatate
- Lutetium Lu 177-dotatate
M
- Maralixibat
- Margetuximab
- Maribavir
- Mavacamten
- Mavenclad
- Mechlorethamine
- Melphalan flufenamide
- Mepolizumab
- Methotrexate
- Metreleptin
- Migalastat
- Migalastat hydrochloride
- Miglustat
- Milrinone
- Mitapivat
- Mitomycin
- Mitomycin Pyelocalyceal
- Mobocertinib
- Mogamulizumab-kpkc
- Mosunetuzumab
- Moxetumomab pasudotox-tdfk
- Moxidectin
- Mycapssa
